Abstract: The present invention relates to a polynucleotide configured for the treatment of a retinal degeneration disease, such as retinitis pigmentosa (RP), a nucleic acid vector comprising said polynucleotide, a pharmaceutical composition comprising said nucleic acid vector, a kit comprising said polynucleotide or said nucleic acid vector, a method of making said nucleic acid vector, and a method for treating a retinal degeneration disease.
Type:
Grant
Filed:
August 22, 2018
Date of Patent:
August 2, 2022
Assignee:
EYESERV GMBH
Inventors:
Stylianos Michalakis, Martin Biel, Mathias Seeliger, Christian Schoen
Abstract: The present invention relates to a polynucleotide configured for the treatment of a disease of retinal cone cells, such as achromatopsia, a nucleic acid vector comprising said polynucleotide, a pharmaceutical composition comprising said nucleic acid vector, a kit comprising said polynucleotide or said nucleic acid vector, a method of making said nucleic acid vector, and a method for treating a disease of the retinal cone cells.
Type:
Grant
Filed:
August 22, 2018
Date of Patent:
December 1, 2020
Assignee:
EyeServ GmbH
Inventors:
Stylianos Michalakis, Martin Biel, Mathias Seeliger