Abstract: Disclosed herein are acyclic thiol prodrugs, and pharmaceutical compositions thereof. The prodrugs and pharmaceutical compositions thereof may be used to treat or prevent medical disorders such as, for example cystinosis, cystinuria, cancer neurodegenerative disease, Parkinson's disease, Huntington's disease, malaria, nonalcoholic fatty liver disease, radiation poisoning, arsenic poisoning, radioprotection, Wilson's disease or rheumatoid arthritis.
Type:
Grant
Filed:
December 28, 2022
Date of Patent:
May 14, 2024
Assignee:
Lilac Therapeutics, Inc.
Inventors:
Manoj Chandrasinhji Desai, Siva R. Kamma
Abstract: Disclosed herein are cyclic thiol prodrugs, and pharmaceutical compositions thereof. The prodrugs and pharmaceutical compositions thereof may be used to treat or prevent medical disorders such as, for example, cystinuria, cystinosis, cancer, neurodegenerative disease, Parkinson's disease, Huntington's disease, malaria, nonalcoholic fatty liver disease, radiation poisoning, arsenic poisoning, radioprotection, Wilson's disease or rheumatoid arthritis.
Type:
Grant
Filed:
December 28, 2022
Date of Patent:
March 19, 2024
Assignee:
Lilac Therapeutics, Inc.
Inventors:
Manoj Chandrasinhji Desai, Siva R. Kamma