Abstract: This disclosure provides compounds, such as compounds of Formula I: pharmaceutical formulations thereof, and related methods of use for the treatment of defects of cholesterol homeostasis including lysosomal storage disorders such as Niemann-Pick Type C disease.
Type:
Grant
Filed:
March 20, 2017
Date of Patent:
January 1, 2019
Assignee:
Perlara PBC
Inventors:
Ethan Oren Perlstein, Nina Di Primio, Tom Aaron Hartl, Sangeetha Venkatraman Iyer, Alexander James Ludin, Tamy May Sharly Portillo Rodriguez, John Alan Tucker
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