Patents Assigned to Rocket Pharmaceuticals, Ltd.
  • Gene therapy vectors for treatment of Danon disease
    Patent number: 10703797
    Abstract: The disclosure relates to optimized polynucleotide sequences for LAMP-2B, expression cassettes, vectors, and methods of use thereof in treating disease, e.g. Danon disease.
    Type: Grant
    Filed: December 27, 2019
    Date of Patent: July 7, 2020
    Assignee: Rocket Pharmaceuticals, Ltd.
    Inventors: Annahita Keravala, Simon Moore, David Ricks
  • GENE THERAPY VECTORS FOR TREATMENT OF DANON DISEASE
    Publication number: 20200148745
    Abstract: The disclosure relates to optimized polynucleotide sequences for LAMP-2B, expression cassettes, vectors, and methods of use thereof in treating disease, e.g. Danon disease.
    Type: Application
    Filed: December 27, 2019
    Publication date: May 14, 2020
    Applicant: Rocket Pharmaceuticals, Ltd.
    Inventors: Annahita KERAVALA, Simon MOORE, David RICKS