Abstract: There is provided a medical agent for use in a method of treatment of nonalcoholic fatty liver disease (NAFLD) or hepatocellular carcinoma (HCC), wherein the medical agent comprises a polynucleotide and is capable of silencing or knocking out the PKLR gene.
Type:
Grant
Filed:
August 14, 2018
Date of Patent:
June 15, 2021
Assignee:
ScandiEdge Therapeutics AB
Inventors:
Adil Mardinoglu, Jan Borén, Mathias Uhién