Abstract: Disclosed herein are compositions and methods related to treating myeloproliferative diseases or disorders, such as MPN, using megakaryocyte-derived extracellular vesicles, including megakaryocyte-derived extracellular vesicles derived from human pluripotent stem cells.
Abstract: Disclosed herein are compositions and methods related to megakaryocyte-derived extracellular vesicles derived from human pluripotent stem cells, where the megakaryocyte-derived extracellular vesicles may be utilized for treating Fanconi anemia (FA).
Type:
Grant
Filed:
April 26, 2022
Date of Patent:
January 13, 2026
Assignee:
STRM.bio Incorporated
Inventors:
Jonathan Thon, David Raiser, Laura Goldberg
Abstract: Disclosed herein are compositions and methods related to megakaryocyte-derived extracellular vesicles derived from human pluripotent stem cells, where the megakaryocyte-derived extracellular vesicles may be utilized for drug delivery and treating various diseases.