Patents Assigned to The Hospital for Sick Chlidren
  • MODULATION OF GYS1 EXPRESSION
    Publication number: 20190194666
    Abstract: Provided herein are methods, compounds, and compositions for reducing expression of GYS1 in an individual. Such methods, compounds, and compositions are useful to treat, prevent, delay, or ameliorate a glycogen storage disease or disorder in an individual in need.
    Type: Application
    Filed: June 19, 2017
    Publication date: June 27, 2019
    Applicants: Ionis Pharmaceuticals, Inc., The Hospital for Sick Chlidren
    Inventors: Tamar R. Grossman, Susan M. Freier, Berge Minassian, Saija Ahonen