Abstract: The present application relates to sialylated glycoprotein compositions and methods of their use in treating various conditions and disorders.
Type:
Grant
Filed:
September 10, 2015
Date of Patent:
October 4, 2016
Assignee:
Ultragenyx Pharmaceutical Inc.
Inventors:
Steven Jungles, Gabrielle Morris, Jeff Grubb, Michael Vellard, Emil D. Kakkis
Abstract: The present application relates to sialylated glycoprotein compositions and methods of their use in treating various conditions and disorders.
Type:
Grant
Filed:
March 5, 2015
Date of Patent:
October 4, 2016
Assignee:
Ultragenyx Pharmaceutical Inc.
Inventors:
Steven Jungles, Gabrielle Morris, Jeff Grubb, Michael Vellard, Emil D. Kakkis
Abstract: The present invention relates to methods of monitoring and assessing sialic acid deficiency treatment as well as to methods of predicting/determining responsiveness to treatment for a sialic acid deficiency using biomarkers. Sialic acid deficiencies include for example Hereditary Inclusion Body Myopathy (HIBM).
Abstract: The present invention relates to methods of monitoring and assessing sialic acid deficiency treatment as well as to methods of predicting/determining responsiveness to treatment for a sialic acid deficiency using biomarkers. Sialic acid deficiencies include for example Hereditary Inclusion Body Myopathy (HIBM).