Patents Examined by Robert Mondes
  • Therapeutic strategies to treat CNS pathology in mucopolysaccharidoses
    Patent number: 9487766
    Abstract: The invention provides for nucleotide sequences encoding for a chimeric sulfatase, viral vectors expressing such sequences for gene therapy and pharmaceutical uses of the chimeric expressed protein. The invention is particularly applied in the therapy of mucopolysaccharidosis, preferably type IIIA.
    Type: Grant
    Filed: November 12, 2015
    Date of Patent: November 8, 2016
    Assignee: FOND AZIONE TELETHON
    Inventors: Andrea Ballabio, Alessandro Fraldi