Patents by Inventor Shire Human Genetic Therapies, Inc.

Shire Human Genetic Therapies, Inc. has filed for patents to protect the following inventions. This listing includes patent applications that are pending as well as patents that have already been granted by the United States Patent and Trademark Office (USPTO).

  • LIVER SPECIFIC DELIVERY OF MESSENGER RNA
    Publication number: 20130195967
    Abstract: Disclosed herein are compositions and methods of modulating the expression of gene or the production of a protein by transfecting target cells with nucleic acids. The compositions disclosed herein demonstrate a high transfection efficacy and are capable of ameliorating diseases associated with protein or enzyme deficiencies.
    Type: Application
    Filed: March 13, 2013
    Publication date: August 1, 2013
    Applicant: Shire Human Genetic Therapies, Inc.
    Inventor: Shire Human Genetic Therapies, Inc.
  • BIOMARKERS FOR SANFILIPPO SYNDROME AND USES THEREOF
    Publication number: 20130121984
    Abstract: The present invention provides biomarkers for efficient and accurate characterization of Sanfilippo syndrome. In particular, the present invention provides biomarkers differentially expressed in Sanfilippo syndrome. Those biomarkers, used alone or in combination, may permit more accurate robust characterization of Sanfilippo syndrome, resulting in more precise determination of the types and/or severity of the syndrome. In addition, inventive biomarkers according to the present invention can be used to effective monitor treatment response in Sanfilippo syndrome patients and/or to optimize treatment for Sanfilippo syndrome.
    Type: Application
    Filed: November 7, 2012
    Publication date: May 16, 2013
    Applicant: SHIRE HUMAN GENETIC THERAPIES, INC.
    Inventor: Shire Human Genetic Therapies, Inc.